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s cells amp。 tissues ? a defective mutant allele is replaced with a functional one How it works ? “normal” gene patient’s “abnormal” one ? target cells by a vector ? retroviruses ? adenoviruses ? adenoassociated viruses ? herpes simplex viruses Development ? 2022, UCLA, potential treatment for Parkinson’s disease ? 2022,National Institutes of Health, killer Tcell helped treat cancer ? 2022, Moorfields Eye Hospital and University College London’s Institute of Ophthalmology, first gene therapy trial for inherited retinal disease. Debate Pros ?